Stakeholders’ feedback on the proposed recommendations for updating the Patented Medicine Prices Review Board (PMPRB) budget impact analysis (BIA) guidelines

Naghmeh Foroutan; Jean-Eric  Tarride; Feng  Xie; Bismah Jameel BS; Fergal  Mills; Mitchell Levine

doi:10.15586/jptcp.v27i1.651

Naghmeh Foroutan

Department of Health Research Methods, Evidence and Impact (HEI), McMaster University, Hamilton, ON, Canada; Programs for Assessment of Technology in Health (PATH), The Research Institute of St. Joe’s, St Joseph’s Healthcare Hamilton, Hamilton, ON, Canada.

Jean-Eric Tarride

Department of Health Research Methods, Evidence and Impact (HEI), McMaster University, Hamilton, ON, Canada; Programs for Assessment of Technology in Health (PATH), The Research Institute of St. Joe’s, St Joseph’s Healthcare Hamilton, Hamilton, ON, Canada; Centre for Health Economics and Policy Analysis (CHEPA), McMaster University, Hamilton, ON, Canada.

Feng Xie

Department of Health Research Methods, Evidence and Impact (HEI), McMaster University, Hamilton, ON, Canada; Centre for Health Economics and Policy Analysis (CHEPA), McMaster University, Hamilton, ON, Canada; Program for Health Economics and Outcome Measures (PHENOM), Hamilton, ON, Canada.

Bismah Jameel BS

Department of Health Research Methods, Evidence and Impact (HEI), McMaster University, Hamilton, ON, Canada.

Fergal Mills

Innomar Consulting, Oakville, ON, Canada.

Mitchell Levine

Department of Health Research Methods, Evidence and Impact (HEI), McMaster University, Hamilton, ON, Canada; Programs for Assessment of Technology in Health (PATH), The Research Institute of St. Joe’s, St Joseph’s Healthcare Hamilton, Hamilton, ON, Canada; Centre for Health Economics and Policy Analysis (CHEPA), McMaster University, Hamilton, ON, Canada.

Keywords

Stakeholder analysis, Public drug plans, Private payers, Pharmaceutical industry, PMPRB budget impact analysis guidelines

Abstract

Introduction: The present study aimed to obtain Canadian stakeholders’ feedback on a list of proposed recommendations for updating the Patented Medicine Prices Review Board (PMPRB)’s 2007 budget impact analysis (BIA) guidelines.

Methods: A mixed-methods study was designed to obtain feedback from two stakeholder perspectives- (public and private) payers and manufacturers- on the proposed BIA recommendations. We obtained policy-makers’ opinions through one-on-one interviews and collected feedback from manufacturers and their consultants using a survey. The interview guide and the survey were developed based on the list of recommendations related to BIA key elements, which were either not discussed or addressed differently in the PMPRB 2007 BIA guidelines. The list was derived from sixteen Canadian or other national and transnational BIA guidelines. A thematic analysis was applied for the analysis of the qualitative (interview) data.

Results: Thirty-five policymakers and manufacturers participated in the study. Stakeholders supported the inclusion 56% of proposed recommendations into the guidelines pertaining to the use of expert opinions, data extrapolated from the payers’ database, scenario analysis, and dynamic population. Inclusion of indirect costs and cost transfers from other jurisdictions were not approved. There was no consensus regarding the inclusion of patients’ adherence/compliance and cost offsets.

Conclusions: The present study has provided sufficient insights to enable the creation of a penultimate version for updating the PMPRB BIA guidelines. This penultimate version will be subject to a broader consultation among stakeholders prior to a final revision and approval. Further Canadian stakeholder feedback is required for reaching consensus on inconclusive recommendations.

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Published

Jan 3, 2020

DOI https://doi.org/10.15586/jptcp.v27i1.651

How to Cite

Foroutan, N., Tarride, J.-E. ., Xie, F. ., Jameel BS, B., Mills, F., & Levine, M. (2020). Stakeholders’ feedback on the proposed recommendations for updating the Patented Medicine Prices Review Board (PMPRB) budget impact analysis (BIA) guidelines. Journal of Population Therapeutics and Clinical Pharmacology, 27(1), e1-e24. https://doi.org/10.15586/jptcp.v27i1.651