Peterson, Robert G, Stuart M MacLeod, and Agnes V Klein. “A New Toolkit for Conducting Clinical Trials in Rare Disorders: Will This Dog Hunt?”. Journal of Population Therapeutics and Clinical Pharmacology 21, no. 1 (November 19, 2018). Accessed July 16, 2024. https://jptcp.com/index.php/jptcp/article/view/346.