ABRAHAMYAN, Lusine; DIAMOND, Ivan R; JOHNSON, Sindhu R; FELDMAN, Brian M. A New Toolkit for Conducting Clinical Trials in Rare Disorders. Journal of Population Therapeutics and Clinical Pharmacology, [S. l.], v. 21, n. 1, 2018. Disponível em: https://jptcp.com/index.php/jptcp/article/view/345. Acesso em: 19 sep. 2025.